These smaller population “Orphan Diseases,” defined as those that affect less than 200,000 people across the U.S., collectively impact 25 million Americans. This substantial public health issue warrants Lancet's call-to-action.
It is Game On! for President Trump appointee Scott Gottlieb, the commissioner of the Food and Drug Administration. Things are definitely changing there, and at this point, it's a pretty good start.
